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Project # Contact PI Funding Organization Fiscal Year
ESTABLISHING FUNCTION OF UNDERSTUDIED PRKCQ KINASE IN CELLULAR REGULATION AND DISEASE
1R03TR002914-01 NEWTON, ALEXANDRA C. NCATS 2019
6TH INTERNATIONAL RASOPATHIES SYMPOSIUM: PRECISION MEDICINE - FROM PROMISE TO PRACTICE
1R13TR002780-01 SCHOYER, LISA NCATS 2019
LUM-001 AS A TREATMENT FOR CREATINE TRANSPORTER DEFICIENCY
1ZIATR000006-05 OTTINGER, ELIZABETH NCATS 2019
USE OF RAPAMYCIN FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY IN PATIENTS WITH NOONAN SYNDROME WITH MULTIPLE LENTIGINES (NSML)
1ZIATR000012-05 OTTINGER, ELIZABETH NCATS 2019
SHORT STABILIZED EPO-PEPTIDE AS THERAPEUTIC AGENTS FOR MULTIPLE SCLEROSIS AND ACUTE BRAIN TRAUMA
1ZIATR000024-05 ALIMARDANOV, ASAF NCATS 2019
DEVELOPMENT OF NOGO RECEPTOR DECOY FOR THE TREATMENT OF SPINAL CORD INJURY
1ZIATR000031-05 ALIMARDANOV, ASAF NCATS 2019
A DRUG-SCREENING PLATFORM FOR AUTISM SPECTRUM DISORDERS USING HUMAN NEURONS AND ASTROCYTES
1ZIATR000073-04 SOUTHALL, NOEL NCATS 2019
IDENTIFICATION OF SMALL MOLECULE INHIBITORS OF MIR-155 EXPRESSION IN TH17 CELLS
1ZIATR000077-05 FERRER-ALEGRE, MARC NCATS 2019
A DRUG BASED APPROACH FOR INTEGRIN-MEDIATED ALLEVIATION FOR MUSCULAR DYSTROPHY
1ZIATR000229-04 MARUGAN, JUAN NCATS 2019
PEROXISOME BIOGENESIS DISORDERS (PBDS)
1ZIATR000246-04 INGLESE, JAMES NCATS 2019