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Project # Contact PI Funding Organization Fiscal Year
ESTABLISHING FUNCTION OF UNDERSTUDIED PRKCQ KINASE IN CELLULAR REGULATION AND DISEASE
1R03TR002914-01 NEWTON, ALEXANDRA C. NCATS 2019
6TH INTERNATIONAL RASOPATHIES SYMPOSIUM: PRECISION MEDICINE - FROM PROMISE TO PRACTICE
1R13TR002780-01 SCHOYER, LISA NCATS 2019
LUM-001 AS A TREATMENT FOR CREATINE TRANSPORTER DEFICIENCY
1ZIATR000006-05 OTTINGER, ELIZABETH NCATS 2019
USE OF RAPAMYCIN FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY IN PATIENTS WITH NOONAN SYNDROME WITH MULTIPLE LENTIGINES (NSML)
1ZIATR000012-05 OTTINGER, ELIZABETH NCATS 2019
A DRUG-SCREENING PLATFORM FOR AUTISM SPECTRUM DISORDERS USING HUMAN NEURONS AND ASTROCYTES
1ZIATR000073-04 SOUTHALL, NOEL NCATS 2019
A DRUG BASED APPROACH FOR INTEGRIN-MEDIATED ALLEVIATION FOR MUSCULAR DYSTROPHY
1ZIATR000229-04 MARUGAN, JUAN NCATS 2019
GENE THERAPY PLATFORM FOR RARE DISEASES
1ZIATR000281-03 YANG, NA NCATS 2019
IDENTIFYING SELECTIVE USP16 INHIBITORS TO SUSTAIN STEM CELL PROLIFERATION
1ZIATR000324-03 SIMEONOV, ANTON NCATS 2019
BPN14770 FOR TREATMENT OF FRAGILE X SYNDROME
1ZIATR000374-01 LO, DONALD NCATS 2019
UNIVERSITY OF PITTSBURGH CLINICAL AND TRANSLATIONAL SCIENCE INSTITUTE
3UL1TR001857-04S1 REIS, STEVEN E NCATS 2019