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Project # Contact PI Funding Organization Fiscal Year
THERAPEUTIC MODULATION OF MYOTONIC MUSCULAR DYSTROPHY
5R37NS094393-04 THORNTON, CHARLES A NINDS 2018
IMPROVING MPS I ERT EFFICACY THROUGH LECTIN-MEDIATED DELIVERY
5R44NS102086-02 RADIN, DAVID NINDS 2018
BIOSTATISTICS AND DATA MANAGEMENT FOR A TRIAL OF CORTICOSTEROID REGIMENS IN DMD
5U01NS061795-08 MCDERMOTT, MICHAEL P NINDS 2018
FOR-DMD: DOUBLE-BLIND RANDOMIZED TRIAL TO OPTIMIZE STEROID REGIMEN IN DUCHENNE MD
5U01NS061799-08 GRIGGS, ROBERT C NINDS 2018
SUDEP RESEARCH ALLIANCE: IPSC AND MOUSE NEUROCARDIAC MODELS, APPLICATION 6 OF 7
5U01NS090364-05 PARENT, JACK M NINDS 2018
PREVENTING EPILEPSY USING VIGABATRIN IN INFANTS WITH TUBEROUS SCLEROSIS COMPLEX
5U01NS092595-03 BEBIN, MARTINA NINDS 2018
HIGH-DOSE ERYTHROPOIETIN FOR ASPHYXIA AND ENCEPHALOPATHY (HEAL) CCC
5U01NS092764-03 WU, YVONNE W NINDS 2018
EFFECTS OF AFQ056 ON LANGUAGE LEARNING IN YOUNG CHILDREN WITH FRAGILE X SYNDROME (FXS)
5U01NS096767-03 BERRY-KRAVIS, ELIZABETH MARA NINDS 2018
CLINICAL TRIAL READINESS TO SOLVE BARRIERS TO DRUG DEVELOPMENT IN FSHD
5U01NS101944-02 TAWIL, RABI NINDS 2018
FUNCTIONAL CHARACTERIZATION OF A CAUSATIVE GENE FOR INTELLECTUAL DISABILITY
7R01NS091220-05 KIM, WOO-YANG NINDS 2018