|
THERAPEUTIC MODULATION OF MYOTONIC MUSCULAR DYSTROPHY |
5R37NS094393-04 |
THORNTON, CHARLES A |
NINDS |
2018 |
|
IMPROVING MPS I ERT EFFICACY THROUGH LECTIN-MEDIATED DELIVERY |
5R44NS102086-02 |
RADIN, DAVID |
NINDS |
2018 |
|
BIOSTATISTICS AND DATA MANAGEMENT FOR A TRIAL OF CORTICOSTEROID REGIMENS IN DMD |
5U01NS061795-08 |
MCDERMOTT, MICHAEL P |
NINDS |
2018 |
|
FOR-DMD: DOUBLE-BLIND RANDOMIZED TRIAL TO OPTIMIZE STEROID REGIMEN IN DUCHENNE MD |
5U01NS061799-08 |
GRIGGS, ROBERT C |
NINDS |
2018 |
|
SUDEP RESEARCH ALLIANCE: IPSC AND MOUSE NEUROCARDIAC MODELS, APPLICATION 6 OF 7 |
5U01NS090364-05 |
PARENT, JACK M |
NINDS |
2018 |
|
PREVENTING EPILEPSY USING VIGABATRIN IN INFANTS WITH TUBEROUS SCLEROSIS COMPLEX |
5U01NS092595-03 |
BEBIN, MARTINA |
NINDS |
2018 |
|
HIGH-DOSE ERYTHROPOIETIN FOR ASPHYXIA AND ENCEPHALOPATHY (HEAL) CCC |
5U01NS092764-03 |
WU, YVONNE W |
NINDS |
2018 |
|
EFFECTS OF AFQ056 ON LANGUAGE LEARNING IN YOUNG CHILDREN WITH FRAGILE X SYNDROME (FXS) |
5U01NS096767-03 |
BERRY-KRAVIS, ELIZABETH MARA |
NINDS |
2018 |
|
CLINICAL TRIAL READINESS TO SOLVE BARRIERS TO DRUG DEVELOPMENT IN FSHD |
5U01NS101944-02 |
TAWIL, RABI |
NINDS |
2018 |
|
FUNCTIONAL CHARACTERIZATION OF A CAUSATIVE GENE FOR INTELLECTUAL DISABILITY |
7R01NS091220-05 |
KIM, WOO-YANG |
NINDS |
2018 |