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INVESTIGATING THE ROLE OF BCKDK IN NEURODEVELOPMENTAL DISORDERS THROUGH A NOVEL MOUSE MODEL |
1R03TR002907-01 |
CHAHROUR, MARIA |
NCATS |
2019 |
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ESTABLISHING FUNCTION OF UNDERSTUDIED PRKCQ KINASE IN CELLULAR REGULATION AND DISEASE |
1R03TR002914-01 |
NEWTON, ALEXANDRA C. |
NCATS |
2019 |
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6TH INTERNATIONAL RASOPATHIES SYMPOSIUM: PRECISION MEDICINE - FROM PROMISE TO PRACTICE |
1R13TR002780-01 |
SCHOYER, LISA |
NCATS |
2019 |
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SYSTEMIC CHARACTERIZATION OF NOVEL LIPIDATED SIRNA CONJUGATES |
1R43TR002791-01 |
SUCKOW, ARTHUR THOMAS |
NCATS |
2019 |
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LUM-001 AS A TREATMENT FOR CREATINE TRANSPORTER DEFICIENCY |
1ZIATR000006-05 |
OTTINGER, ELIZABETH |
NCATS |
2019 |
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USE OF RAPAMYCIN FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY IN PATIENTS WITH NOONAN SYNDROME WITH MULTIPLE LENTIGINES (NSML) |
1ZIATR000012-05 |
OTTINGER, ELIZABETH |
NCATS |
2019 |
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A DRUG-SCREENING PLATFORM FOR AUTISM SPECTRUM DISORDERS USING HUMAN NEURONS AND ASTROCYTES |
1ZIATR000073-04 |
SOUTHALL, NOEL |
NCATS |
2019 |
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A DRUG BASED APPROACH FOR INTEGRIN-MEDIATED ALLEVIATION FOR MUSCULAR DYSTROPHY |
1ZIATR000229-04 |
MARUGAN, JUAN |
NCATS |
2019 |
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GENE THERAPY PLATFORM FOR RARE DISEASES |
1ZIATR000281-03 |
YANG, NA |
NCATS |
2019 |
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IDENTIFYING SELECTIVE USP16 INHIBITORS TO SUSTAIN STEM CELL PROLIFERATION |
1ZIATR000324-03 |
SIMEONOV, ANTON |
NCATS |
2019 |